Columnist Betty Vertin says her youngest daughter is starting to become aware of her older brothers' health challenges with DMD.

RGX-202, a DMD gene therapy, has been well tolerated in an ongoing clinical trial and improved motor function for DMD boys, per interim data.

Columnist Shalom Lim is sad to say goodbye to his caregiver of 18 years, but looks forward to the new chapter of life this ...

A young man with Duchenne MD and treated with Elevidys has died of acute liver failure, Sarepta reports; it's working with ...

Preventive treatment with standard heart medications — when given before the onset of cardiac troubles — extends survival among males with Duchenne muscular dystrophy (DMD), according to data from the ...

Capricor Therapeutics’ investigational therapy deramiocel (CAP-1002) is being considered for approval in the U.S.

Columnist Betty Vertin has a day of heightened awareness about her sons' experience with wheelchairs and life with DMD.

An onslaught of new setbacks due to FSHD disease progression has left columnist Robin Stemple understandably anxious about ...