Rett syndrome is a rare neurodegenerative disorder that almost exclusively affects girls. It is typically diagnosed in babies ...
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Neurogene Begins Dosing in Rett Syndrome Trial
Neurogene ( ($NGNE) ) just unveiled an update. On November 6, 2025, Neurogene Inc. announced the dosing of the first participant in the Embolden™ ...
NEW YORK - Neurogene Inc. (NASDAQ:NGNE), a clinical-stage biotech company with a market capitalization of $368 million, has completed discussions with the U.S. Food and Drug Administration on its ...
Previously disclosed 100% response rate across all 10 patients in Part A for pivotal trial primary endpoint of gain/regain of ≥ one natural history defined developmental milestone assessed via ...
New preclinical data at ESGCT Congress highlight NGN-401 best-in-class potential and add to body of evidence that ICV administration is superior to IT-L in reaching key brain regions underlying Rett ...
More than 130 people gathered at Fontaine Field in Norwich Oct. 11 for a community walk supporting individuals with Down Syndrome. The event marked the first annual Step Up Walk for Down Syndrome in ...
The government-backed Public Provident Fund (PPF) is well-liked for its guaranteed returns, making it a preferred choice among conservative investors. You can easily open a PPF account at designated ...
‘Restoring levels of the molecule pleiotrophin could be a key to repairing or enhancing brain function in people with #Downsyndrome! #DownSyndromeResearch #BrainHealth’ Pleiotrophin's Role in Down ...
Journal Editorial Report: A call to return to the ‘warrior ethos.’ President Trump took another step down the only path to peace in Ukraine when he said Sunday that “if this war is not going to get ...
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