The FDA's decision follows data from a Phase Ib study on salanersen.

Designation is supported by an exploratory analysis from the Phase 1b study showing that some children with SMA previously treated with gene ...

Biogen BIIB recently announced that the FDA has granted Breakthrough Therapy designation to Salanersen, an investigational ...

Peter L. Salgo, MD: Now we’re going to look at something called spinal muscular atrophy [SMA]. I must tell you that before researching it for this broadcast, it was not a disease that was on my radar.

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

Forbes contributors publish independent expert analyses and insights. Spinal muscular atrophy affects the nerves that control muscle movement, leading to progressive weakening. As a result, infants ...

MEDICINES for babies with spinal muscular atrophy will be funded by the NHS for all patients for the first time. Little Mix singer Jesy Nelson’s twins have the condition, also known as SMA. It is ...

"Managing pain in patients with SMA begins with the recognition that there are predictable etiologies leading to pain in SMA and investigating them during each medical visit is important to implement ...

If you’ve done prenatal testing and found out that your baby has spinal muscular atrophy (SMA), it’s normal to feel overwhelmed. Educating yourself about the condition can help you understand what to ...

The risk of scoliosis was largely related to what type of SMA a patient had, with those with type III having the lowest risk and those with type II developing scoliosis at a later age than those with ...

A local family has a personal stake in the donations that pour into St. Jude Children’s Research Hospital. Every month, the ...

Spinal muscular atrophy (SMA) and spina bifida are distinct conditions that affect the nerves that allow for voluntary motor control. Share on Pinterest press coverage photography/Getty Images SMA is ...