Comedian Gilbert Gottfried, shown in a 2016 photo, died on Tuesday, April 12, from recurrent ventricular tachycardia due to myotonic dystrophy type II. Scott Roth Scott Roth/Invision/AP Comedian ...

Myotonic dystrophy type 1 incurs high healthcare costs, driven by age and comorbidities like cardiac and respiratory issues. Early detection and integrated management of multisystemic complications ...

AOC 1001 continues to be generally well tolerated; Avidity provides more information on the rare serious adverse event in a single participant that led to the partial clinical hold AOC 1001 top-line ...

- Patient-reported outcomes support clinical meaningfulness of improvements in function and strength - - Meaningful improvements in overall disease burden reported by both patients and physicians - ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Back to Healio A Southern California biopharmaceutical ...

Please provide your email address to receive an email when new articles are posted on . The FDA has granted breakthrough therapy designation to a proprietary oligonucleotide conjugate for the ...

Dyne Therapeutics announces FDA Fast Track designation for DYNE-101, targeting myotonic dystrophy type 1 with potential accelerated approval in 2026. Dyne Therapeutics has announced that its ...

Comedian Gilbert Gottfried died on Tuesday after a long illness, his family announced. His publicist revealed in a statement to multiple publications, including People, that Gottfried had “recurrent ...