A LAYTOWN family is racing against time to raise €2.7 million for life-changing treatment in the United States for their ...

Capricor has reapplied for FDA approval of deramiocel, its therapy for DMD-related heart disease, and expects a decision by August 22.

"My medicine is making me stronger," 7-year-old Hudson Sanford says after receiving a breakthrough gene therapy for Duchenne Muscular Dystrophy Cara Lynn Shultz is a writer-reporter at PEOPLE. Her ...

The two boys both have Duchenne Muscular Dystrophy, a genetic disorder that typically has children wheelchair bound by the age of 12. Average life expectancy is less than 30. But there is a gene ...

A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular dystrophy (DMD), after the treatment failed to show significant benefit in a ...

A charity transforms a garden in Brierley Hill for two brothers with Duchenne Muscular Dystrophy.

Solid Biosciences’ SGT-003 is the only late‑stage program to show early cardiac benefit across biomarkers and function, according to William Blair.

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

From Philly and the Pa. suburbs to South Jersey and Delaware, what would you like WHYY News to cover? Let us know! Yuva Gambhir has a full life. The University of Pennsylvania senior studies cognitive ...

BRAINERD — Motorcycle riders and enthusiasts from across the world will soon descend on Brainerd as they work to raise awareness and fight Duchenne muscular dystrophy. Hosted by Brainerd's Craig ...